Gene therapy is an experimental technique that uses genes to treat or prevent disease. This technique allow doctors to treat a disorder by inserting or correcting a gene into a patient’s cells instead of using drugs or surgery. Several approaches exist for gene therapy such as:
Compensating a mutated gene that causes disease with a healthy copy of the gene.
Correcting or inactivating a mutated gene that is functioning improperly.
Introducing a new gene into the body to help fight a disease.
The critical importance of validation
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